{"disease":{"id":"asymptomatic-carrier-state","name":"asymptomatic carrier state"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT06360289","title":"Observational Study of Neurofilament Light Chain (NfL) as a Biomarker in Asymptomatic Carriers of the Transthyretin (TTR) Variants and Patients With Hereditary Transthyretin-mediated (hATTR) Amyloidosis With Polyneuropathy","phase":"","overall_status":"RECRUITING","enrollment_count":500,"lead_sponsor_name":"Alnylam Pharmaceuticals","has_results":false}],"total":1},"guidelines":[],"source":"Drug Landscape verified database"}