{"disease":{"id":"aspartylglucosamidase-aga-deficiency","name":"aspartylglucosamidase aga deficiency"},"drugs":{"marketed":[],"pipeline":[],"offLabel":[],"totalMarketed":0,"totalPipeline":0},"trials":{"data":[{"nct_id":"NCT07530796","title":"Safety and Efficacy of scAAV9/AGA Gene Therapy in Participants With Aspartylglucosaminuria (AGU)","phase":"PHASE1, PHASE2","overall_status":"NOT_YET_RECRUITING","enrollment_count":9,"lead_sponsor_name":"Rare Trait Hope","has_results":false},{"nct_id":"NCT03853876","title":"A Natural History Study of Aspartylglucosaminuria","phase":"","overall_status":"TERMINATED","enrollment_count":8,"lead_sponsor_name":"Neurogene Inc.","has_results":false}],"total":2},"guidelines":[],"source":"Drug Landscape verified database"}